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Overview

Our Modalities.

CELL

Programmable CAR-T cells

13 programs

GENE

CRISPR gene editing

5 programs

RNA

RNA therapeutics

12 programs

DLVR

Gene delivery

7 programs

BIO

AI-guided biologics

7 programs

MOL

AI-generated small molecule

8 programs


OUR PIPELINE

Six Modalities. Four Gates. One Platform.

52 programs

Channel

01 · DISCOVERY

Target and lead identification

02 · PRECLINICAL

Safety and efficacy models

03 · IND-ENABLING

Tox, PK, CMC for filing

04 · CLINICAL

In human

CELLProgrammable CAR-T cells13 programs
GENECRISPR gene editing5 programs
RNARNA therapeutics12 programs
DLVRGene delivery7 programs
BIOAI-guided biologics7 programs
MOLAI-generated small molecule8 programs
CELL Programmable CAR-T cells

BCMA

Multiple myeloma

STAGE

Phase I/II

FIRST IN HUMAN

2025

MODALITY

Ex Vivo CAR-T (3rd-gen)

AREA

Oncology / Hematology

STAGE INTENSITY

Discovery
Preclinical
IND-enabling
Clinical

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